This study looks at boys with Duchenne muscular dystrophy (DMD) to check for special antibodies in their blood. Antibodies are proteins made by the body to help fight infections. The specific antibody being studied is called anti-adeno-associated serotype 8 (AAV8). This is an observational screening study, which means doctors will only look at your blood to find out if you have these antibodies.
- It involves a phone or video call for consent and medical history.
- A single visit from a healthcare worker to your home to take a small blood sample.
- Another phone or video call to share the test results with you.
To participate, boys must be younger than 12 years old, have DMD, and provide a signed consent form. Boys who have been in a gene therapy trial or had a gene therapy drug before cannot join. This study may help doctors find boys who can take part in future gene therapy trials for DMD. There are no treatments or medications involved, just a simple blood test. Talk to your doctor if you're interested!