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NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

Clinical trial for boys with Duchenne Muscular Dystrophy.

Recruiting
4-14 years
Male
Phase 2
  • Simplified description (AI rewritten)
  • Technical description (Original)

Study for Boys with Duchenne Muscular Dystrophy (DMD): This research focuses on boys aged 4 to 15 with a specific type of DMD, a genetic disorder that weakens muscles. The study tests a new drug, NS-089/NCNP-02, given through an IV (a tube that goes into a vein) once a week. The drug is designed to help boys with certain gene mutations.

The study has two parts. In Part 1, 6 boys will try the drug. In Part 2, 14 more boys will join. To be in the study, boys must be able to walk and perform a specific standing test without help. They also need to be on a stable dose of a medicine called glucocorticoid for 3 months. Boys who weigh less than 20 kg, have heart problems, or have had certain treatments recently cannot join.

  • The study involves weekly visits for the drug infusion.
  • Participants must be able to walk and stand without help.
  • Some medical history may prevent participation.

Understanding the study helps decide if it's the right fit for you or your child.

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Study details
    Duchenne Muscular Dystrophy

NCT05996003

NS Pharma, Inc.

7 June 2025

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