Study for Boys with Duchenne Muscular Dystrophy (DMD): This research focuses on boys aged 4 to 15 with a specific type of DMD, a genetic disorder that weakens muscles. The study tests a new drug, NS-089/NCNP-02, given through an IV (a tube that goes into a vein) once a week. The drug is designed to help boys with certain gene mutations.

The study has two parts. In Part 1, 6 boys will try the drug. In Part 2, 14 more boys will join. To be in the study, boys must be able to walk and perform a specific standing test without help. They also need to be on a stable dose of a medicine called glucocorticoid for 3 months. Boys who weigh less than 20 kg, have heart problems, or have had certain treatments recently cannot join.

• The study involves weekly visits for the drug infusion.
• Participants must be able to walk and stand without help.
• Some medical history may prevent participation.

Understanding the study helps decide if it's the right fit for you or your child.